Isogenic GAA-KO Murine Muscle Cell Lines Mimicking Severe Pompe Mutations as Preclinical Models for the Screening of Potential Gene Therapy Strategies

Artículo original

Año: 2022

Aguilar-Gonzalez, A; Gonzalez-Correa, JE; Barriocanal-Casado, E; Ramos-Hernandez, I; Lerma-Juarez, MA; Greco, S; Rodriguez-Sevilla, JJ; Molina-Estevez, FJ; Montalvo-Romeral, V; Ronzitti, G; Sanchez-Martin, RM; Martin, F; Munoz, P

Título: INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES

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